Revolutionizing Inner Ear Disorders Therapeutics with Novel Gene Therapy for Replacement of Lost Hair Cells in Rare Genetic Hearing Loss
Time: 10:00 am
day: Conference Day 1
Details:
- Positive clinical results for transformative AAV-based gene therapy to restore and improve hearing loss for inherited hearing loss
- Preclinical results showcasing safety profiles of novel gene therapy targeting OTOF deficiency
- Discovering new protein recombinant-based otoferlin therapy to restore normal gene function in mutated mouse models
